Companies related to orphan diseases

Alone we are rare. Together we are strong.®

Always Ahead

First-in-kind stem cell therapy to combat neurodegenerative diseases, giving back treatment perspective to millions

DRG Turns Physician-Made Clinical Discoveries Into Accessible Drugs

FOR RARE, BY RARE

Tenacious in our search for transformative therapies

AOP Health is the European pioneer for integrated therapies for rare diseases and in critical care.

Supply chain specialist for rare & orphan diseases' medicines in the pharmaceutical industry

Specialty Plasma-Derived Therapeutics

We are a late-stage biopharmaceutical company focused on developing & commercializing products to treat rare diseases

Shifting the treatment paradigm for neurodegenerative disease towards precision medicine and disease prevention.

aTyr is a biotherapeutics company engaged in the development of innovative medicines based on novel biology.

Healing the disease that causes cancer