Eloxx Pharmaceuticals

Eloxx Pharmaceuticals

Biotechnology-Research

Watertown, Massachus...
United States
Company Tagline

Clinical-stage biopharma company developing novel RNA-modulating drug candidates to treat rare and ultra rare diseases.

Industry Category
Biotechnology-Research
Company Description

Eloxx Pharmaceuticals is a pioneering biotechnology research company dedicated to developing innovative RNA-modulating drug candidates for the treatment of rare and ultra-rare premature stop codon diseases. Eloxx Pharmaceuticals is committed to addressing critical unmet needs in genetic diseases through cutting-edge therapeutic development.

Located at 480 Arsenal Way Suite 130, Watertown, Massachusetts 02472, US, Eloxx Pharmaceuticals focuses on extending mRNA half-life and increasing protein synthesis by enabling the cytoplasmic ribosome to read through premature stop codons, ultimately producing full-length proteins. The company’s lead product candidate, ELX-02, is a small molecule drug designed to restore the production of full-length functional proteins and is currently in early-stage clinical development, targeting cystic fibrosis and cystinosis.

Eloxx Pharmaceuticals continues to advance its research and development efforts, striving to make a significant impact on the lives of patients affected by rare genetic disorders. With a strong foundation in biotechnology and a clear focus on RNA modulation, Eloxx Pharmaceuticals is poised for continued growth and innovation in the biopharmaceutical industry. We invite the manager of Eloxx Pharmaceuticals to create a customized and exclusive company showcase and product listing on our platform.

Eloxx Pharmaceuticals est une entreprise pionnière de recherche en biotechnologie dédiée au développement de candidats médicaments novateurs modulant l'ARN pour le traitement des maladies rares et ultra-rares à codon d'arrêt prématuré. Eloxx Pharmaceuticals s'engage à répondre aux besoins critiques non satisfaits dans les maladies génétiques grâce à un développement thérapeutique de pointe.

Située au 480 Arsenal Way Suite 130, Watertown, Massachusetts 02472, États-Unis, Eloxx Pharmaceuticals se concentre sur l'extension de la demi-vie de l'ARNm et l'augmentation de la synthèse des protéines en permettant au ribosome cytoplasmique de lire à travers les codons d'arrêt prématurés, produisant ainsi des protéines de pleine longueur. Le principal candidat produit de la société, ELX-02, est une petite molécule conçue pour restaurer la production de protéines fonctionnelles de pleine longueur et est actuellement en phase précoce de développement clinique, ciblant la mucoviscidose et la cystinose.

Eloxx Pharmaceuticals continue de faire progresser ses efforts de recherche et développement, s'efforçant d'avoir un impact significatif sur la vie des patients atteints de troubles génétiques rares. Avec une base solide en biotechnologie et une orientation claire sur la modulation de l'ARN, Eloxx Pharmaceuticals est prête pour une croissance et une innovation continues dans l'industrie biopharmaceutique. Nous invitons le responsable d'Eloxx Pharmaceuticals à créer une vitrine d'entreprise et une liste de produits personnalisées et exclusives sur notre plateforme.

Key Personnel / Employees
Vasudeo Badarinarayana He “River” Zhao Roger Clark Daniel Geffken Alex Golden Michal Shavit (Head of Pharmaceutical Research) Chaim Eldar (Senior Executive (CPA)|Vast experience in leading business activities in Israel and overseas)

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Compare Eloxx Pharmaceuticals with 3 companies in Biotechnology-Research

4 Companies
Comparison Field
Eloxx Pharmaceuticals
Eloxx Pharmaceuticals
Main Company
Janssen Inc.
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Founded Year
1989 2015
Company Size
501-1,000 51-200 2-10
City
Watertown, Massachusetts Toronto, Ontario Chicago, IL Not Specified, Dubai
Country
United States Canada United States United Arab Emirates
Skills & Keywords Comparing with main company
12 Total Skills
Biopharmaceutical RNA Modulation Genetic Diseases Drug Development Cystic Fibrosis Cystinosis ELX-02 Healthcare Rare Diseases Life Sciences Biotech Pharmaceuticals
1 Total 1 Unique
Unique Skills:
Innovation
25 Total 25 Unique
Unique Skills:
Analytical Beverage Biotechnology Chemical Cosmetics & Personal Care Data Science +19
10 Total 10 Unique
Unique Skills:
Africa Cell Therapies GCC Gene Therapies Market Access Market Research +4
4
Total Companies
1989
Oldest Founded
3
Countries
48
Unique Skills

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Alternative Company Names

This company is also known as

Eloxx Pharmaceuticals एलोक्स फार्मास्युटिकल्स إلوكس للأدوية Элокс Фармасьютикалс